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02142aam a22004098i 4500 001 264C4796A6B511EDAB1CAA9536ECA4DB 003 SILO 005 20230207010047 008 220728s2023 nyu b 001 0 eng 010 $a 2022023324 020 $a 0399576134 020 $a 9780399576133 040 $a DLC $b eng $e rda $c DLC $d DLC $d SILO 050 00 $a RJ399.L95 $b M37 2023 082 00 $2 23/eng/20220802 100 1 $a Marcus, Amy Dockser, $e author. $9 45481 245 10 $a WE THE SCIENTISTS : $b HOW A DARING TEAM OF PARENTS AND DOCTORS FORGED A NEW PATH FOR MEDICINE / $c Amy Dockser Marcus. 250 $a First edition. 263 $a 2302 264 1 $a New York : $b Riverhead Books, $c 2023. 300 $a pages cm 504 $a Includes bibliographical references and index. 520 $a "Pulitzer Prize-winning reporter Amy Dockser Marcus shows what happened when a group of parents joined forces with doctors and researchers to try to save children's lives. Parents whose children had been diagnosed with the rare and fatal genetic conditionNiemann-Pick Type C disease recognized there would never be a treatment in time to save their children if things stayed the same, so the parents set up a collaboration with researchers and doctors in search of a cure. Their social experiment reveals newpathways for treating disease and conducting research"-- $c Provided by publisher. 650 0 $a Niemann-Pick diseases $x Treatment. 650 0 $a Rare diseases $x Patients. 650 0 $a Genetic disorders in children $x Family relationships. $x Family relationships. 650 0 $a Parents of children with disabilities. $9 73773 776 08 $i Online version: 776 08 $a Dockser Marcus, Amy. $t We the scientists $b First edition. $d New York : Riverhead Books, 2023 $z 9780399576157 $w (DLC) 2022023325 941 $a 6 952 $l YEPF572 $d 20240509011625.0 952 $l BOPG851 $d 20231010032552.0 952 $l GBPF771 $d 20230603010744.0 952 $l TCPG826 $d 20230502010408.0 952 $l XXPH787 $d 20230405013438.0 952 $l BAPH771 $d 20230207010135.0 956 $a http://locator.silo.lib.ia.us/search.cgi?index_0=id&term_0=264C4796A6B511EDAB1CAA9536ECA4DBInitiate Another SILO Locator Search